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The NORTHSTAR study is testing the safety, effectiveness, and tolerability of an investigational drug called gildeuretinol acetate (ALK-001) in those with Stargardt disease. Participants who are medically eligible to take part in the study will be randomly assigned to receive either the investigational drug or placebo during the treatment period. The study drug and placebo come in capsule form and are taken by mouth once a day.
You may be able to join if you:
- Are 8 to 45 years old
- Have been diagnosed with typical autosomal recessive Stargardt disease (STGD), a form of inherited macular dystrophy
- Have genetic test results showing at least one disease-causing change (mutation) in the ABCA4 gene
If you or your child choose to participate, the investigational drug and all study-related visits, exams, tests, and procedures that are not part of routine care will be provided at no cost to you.
Email trials@alkeus.com for more information or to see if you qualify.
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