Gene Therapy Research: Understanding the Science
11:30 AM - 12:45 PM
Track: For All
Have questions about gene therapy research? Learn about the goals of gene therapy research, possible risks and eligibility criteria from a leading expert, Guy Young, MD; Director, Hemostasis and Thrombosis Program; Children’s Hospital Los Angeles. This interactive live program will answer questions about gene therapy research, including how gene therapy research is designed to work; what different types of gene therapies are being researched; and why are some people eligible for gene therapy trials while others are not.
No gene therapies have been approved for hemophilia A or B or been determined to be safe or effective.
Sponsored by Biomarin