We are continuing to review the four Pillars that form the foundation of FAST’s Roadmap to Cure 2.0. Again, these recaps will serve as a review of the pillar itself, the progress presented in last year’s Summit, and exciting developments to look forward to at this year’s event.

Learn more about Pillar 2:

The Phase 3 Efficacy and Safety Study of GTX-102 (ASO) in Pediatrics, sponsored by Ultragenyx, is now listed on ClinicalTrials.gov.

Interested in learning more? ASF and FAST will be hosting a community webinar about the trial, named Aspire, with the Ultragenyx team on Oct 23, 2024 at 1:00pm EST. Submit your questions and register below.

Submit your questions and register below:

It was a busy September for our CAN fundraisers! There were five fundraising activities all of a unique nature to raise money for Angelman syndrome! We are so grateful for all of these families and communities for their efforts. Learn more about each event below!

CAN Spotlight: Friends of James

CAN Spotlight: All in for Olin

CAN Spotlight: Granville Angels 

CAN Spotlight: Maddie’s Mission 

CAN Spotlight: Jade’s Bike Ride

The room block for the Global Science Summit & Gala in Orlando, FL closes on October 11! If you haven’t already, be sure to book your hotel room now.

Book your hotel room now:

Did you know that each fall, the Combined Federal Campaign (CFC) enables Federal employees and retirees to donate money through payroll deductions to support their favorite charities? This is an easy way to help advance the mission of FAST on a recurring basis. Visit the CFC to learn more or see the simple steps below:

1. Online Giving System: Click the Donate button at the top of the page to get started.

2. Paper Pledge Form: Download a pledge form and get instructions on how to fill it out and submit it. 

3. Text-to-Donate

4. CFC Giving App

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